Explore the Agenda

7:45 am Check In & Coffee

8:20 am Chair’s Opening Remarks

Strategic Access Planning: Managing Exit Strategies & Reimbursement from Start to Finish

8:30 am Panel Discussion: Planning & Executing Smooth Transitions from EAP to Commercial Supply

Head, Global Independent Medical Education, Investigator Sponsored Trials & US Expanded Access Program, Jazz Pharmaceuticals plc
Assoc Director EAP, Blueprint Medicines
Director, Head of Global Medical Operational Excellence and Strategic Planning, Blueprint Medicines
Associate Director & Senior Manager - Medical Affairs, Global IST Operations, Investigator Sponsored Trial & EAP Operations, Jazz Pharmaceuticals plc
  •  Anticipating patient needs and country-specific timelines to maintain uninterrupted access during program closure or handover
  • Aligning internal teams, local stakeholders, and advocacy groups to address operational, regulatory, and financial challenges
  • Learning from real-world multi-country cases to optimize transition planning and avoid common pitfalls

9:00 am Bridging the Gap Between Regulatory Approval & Commercial Launch: Access Strategies

  • Leveraging flexible access pathways between regulatory approval and commercial launch to provide patients with access while minimising costs
  • Exploring case studies of successful access strategies in Europe, highlighting how companies have navigated multiple access pathways and overcome challenges
  • Identifying cost-saving opportunities in distribution, including localised distribution strategies and reducing reliance on clinical product shipments, without compromising patient access or safety

9:30 am Session Reserved for Inceptua

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10:00 am Morning Break & Networking

11:00 am Rapid Fire Solutions: Building Ethical & Compliant Chargeable Access

Principal, GARDaccess
  • Skip the theory and dive straight into what works. This fast-paced practical session explores real-world approaches to chargeable access through case studies from countries piloting subscription models, tiered pricing, co-pay caps, and other innovative strategies. In interactive exercises, co-design practical access blueprints, testing pricing, eligibility, payer mixes, and ethical safeguards. Leave with actionable frameworks and tools to implement fair, sustainable, and compliant paid access programs in diverse healthcare settings.

Driving Cohesion Across Internal & External Partners for Effective EAPs

11:45 am Clarifying Regulatory & Operational Differences Between Cohort & Individual Patient Programs to Align Program Design with Target Populations

Senior Director - Program & Oncology, Corcept Therapeutics Incorporated
  • Unpacking important distinctions between cohort and individual patient regulatory pathways and impact on program design
  • Exploring cost and resource considerations, including the need for a CRO, which are required to execute cohort and individual patient programs
  • Implementing the obligatory commitments of running a cohort program into the pre-existing company infrastructure

12:15 pm Operating EAPs In-House, Hybrid, or Fully Outsourced: Finding the Right Model

Director, Managed Access Programs, Bristol Myers Squibb
Executive Director - Managed Access, Medical Evidence Generation & Programs Lead, Bristol Myers Squibb
  • Comparing the pros and cons of fully in-house, fully outsourced, and hybrid approaches to program management
  • Leveraging vendor expertise for complex countries or niche therapies while maintaining control over core markets
  • Learning from real-world case studies on outsourcing, internalizing, and transitioning programs smoothly

12:45 pm Lunch & Networking

1:45 pm Session Reserved for Bionical Emas

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2:15 pm The Rationalization of EAPs for Small Biotech

Chief Executive Officer, WinSanTor Inc.
  • Profit, survival or compassionate use • Navigating the evolving Expanded Access Programs globally
  • Discussing the “all-in-one” role by managing regulatory, supply, clinical, and commercial responsibilities simultaneously
  • Establishing priorities and workflows when multiple functions rely on one or two team members
  • Building internal awareness and educating cross-functional teams to secure cooperation and reduce bottlenecks
  • Leveraging vendor partnerships strategically to supplement expertise while maintaining oversight

Advanced Modalities: Delivering Innovative Therapies Through Effective EAPs

2:45 pm Implementing Home Infusion in Early Access Programs: Lessons from a Spinal Muscular Atrophy Case Study

Director - Early Access Program, Scholar Rock Holding Corporation
Associate Director - Global Medical Strategy & Operations, Scholar Rock Holding Corporation
  • Navigating unique challenges of providing infusion therapy in a home setting
  • Addressing operational and regulatory hurdles, including pharmacy manuals, IRB approvals, and agency contracting
  • Engaging physicians and patients while ensuring uptake, satisfaction, and preparing for commercial transition

3:15 pm Afternoon Break & Networking

3:45 pm Gene Therapies: Global Pathways to Bridge Innovation & Access

Global Medical Affairs Head, Orchard Therapeutics
  • Enabling early patient access to investigational gene therapies through global pre-approval pathways and compassionate use programs
  • Supporting patient access to gene therapy treatment with managed and conditional post-approval models
  • Strengthening safety, effectiveness, and global alignment by leveraging multi-stakeholder data and collaboration

4:15 pm Rare & Ultra-Rare Diseases: Designing Programs for Maximum Patient Impact

Vice President - Global Advocacy Relations & Patient Engagement, Savara Pharmaceuticals
  • Navigating patient advocacy pressures, ethical considerations, and access equity
  • Supporting single-patient vs cohort access in a dynamic regulatory environment
  • Applying concrete program design and operational solutions for rare and ultra-rare diseases

4:45 pm Chairs Closing Remarks

4:50 pm End of Conference